Browsing by Subject "Gene therapy"

Now showing items 1-3 of 3

Cardiac Amyloidosis: Evolving Pathogenesis, Multimodal Diagnostics, and Principles of Treatment

Medarametla, Gnana Deepthi; Kahlon, Ripudaman Singh; Mahitha, Lampimukhi; Shariff, Sanobar; Vakkalagadda, Naga Praneeth; Chopra, Hitesh; Kamal, Mohammad Amjad; Patel, Neil; Sethi, Yashendra; Kaka, Nirja (Creative Commons Attribution 4.0 International License., 2023-09-03)

Amyloidosis is a protein deposition disorder in which insoluble fibril structures accumulate in the bodily tissues damaging the organ function. Cardiac amyloidosis is a severe but under-reported medical condition characterized ...
A Review on the Emergence of Adeno-Associated Virus (AAV) for the Management of RETT Syndrome With Improved Safety and Efficacy

Layla, Nowshin (Daffodil International University, 23-05-08)

Rett Syndrome (RTT) is a rare neuronal disorder caused by alteration of MECP2 gene. There is currently no cure for RTT, but gene therapy with adeno-associated virus (AAV) vectors holds great promise as a potential treatment ...
Thalassemia and Cell Based Gene Therapy (Zynteglo)

Rahman, Shazidur (Daffodil International University, 23-05-08)

Thalassemia is a group of inherited blood disorders characterized by decreased or absent production of one or more of the globin chains that make up hemoglobin. It is a major public health problem, particularly in the ...

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